Fulcrum’s 20 mg Pociredir Trial Shows Promising Hemoglobin & Vaso‑Occlusion Benefits in Sickle Cell Disease
Fulcrum Therapeutics’ Phase 1b pociredir trial shows 20 mg boosts hemoglobin and reduces vaso‑occlusive crises in sickle cell disease—early evidence of a promising gene‑regulation therapy.
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